Leslie Weber

Leslie Weber

Memorial Sloan Kettering Cancer Center - Indore / United States
Others
AD Scientific Index ID: 4441567
person_outline Leslie Weber's MOST POPULAR ARTICLES
1-) Gene therapy in a patient with sickle cell diseaseJA Ribeil, S Hacein-Bey-Abina, E Payen, A Magnani, M Semeraro, ...New England Journal of Medicine 376 (9), 848-855, 20176112017
2-) Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locusC Antoniani, V Meneghini, A Lattanzi, T Felix, O Romano, E Magrin, ...Blood, The Journal of the American Society of Hematology 131 (17), 1960-1973, 20181562018
3-) Editing a g-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotypeL Weber, G Frati, T Felix, G Hardouin, A Casini, C Wollenschlaeger, ...Sci. Adv 6, 20201182020
4-) Plerixafor enables safe, rapid, efficient mobilization of hematopoietic stem cells in sickle cell disease patients after exchange transfusionC Lagresle-Peyrou, F Lefrère, E Magrin, JA Ribeil, O Romano, L Weber, ...Haematologica 103 (5), 778-786, 20181172018
5-) An optimized lentiviral vector efficiently corrects the human sickle cell disease phenotypeL Weber, V Poletti, E Magrin, C Antoniani, S Martin, C Bayard, H Sadek, ...Molecular Therapy-Methods & Clinical Development 10, 268-280, 2018292018