Monique Ryan

Monique Ryan

Royal Children's Hospital Melbourne - Parkville / Australia
Others
AD Scientific Index ID: 4924825
person_outline Monique Ryan's MOST POPULAR ARTICLES
1-) Nusinersen versus sham control in infantile-onset spinal muscular atrophyDVDC Finkel RS, Mercuri E, Darras BT, Connolly AM, Kuntz NL, Kirschner J ...N Engl J Med. 377, 201715332017
2-) Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE studyD De Vivo, E Bertini, K Swoboda, WL Hwu, T Crawford, R Finkel, ...Neuromuscular Disorders 29 (11), 20195042019
3-) Ataluren treatment of patients with nonsense mutation dystrophinopathyK Bushby, R Finkel, B Wong, R Barohn, C Campbell, GP Comi, ...Muscle & nerve 50 (4), 477-487, 20145002014
4-) Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort studyCM McDonald, EK Henricson, RT Abresch, T Duong, NC Joyce, F Hu, ...The Lancet 391 (10119), 451-461, 20184822018
5-) Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trialCM McDonald, C Campbell, RE Torricelli, RS Finkel, KM Flanigan, ...The Lancet 390 (10101), 1489-1498, 20174762017