Phillip A Doerfler

Phillip A Doerfler

St. Jude Children's Research Hospital - Memphis / United States
Natural Sciences / Molecular Biology & Genetics
AD Scientific Index ID: 4609355
person_outline Phillip A Doerfler's MOST POPULAR ARTICLES
1-) Chromothripsis as an on-target consequence of CRISPR–Cas9 genome editingML Leibowitz, S Papathanasiou, PA Doerfler, LJ Blaine, L Sun, Y Yao, ...Nature genetics 53 (6), 895-905, 20211632021
2-) Genome editing of HBG1 and HBG2 to induce fetal hemoglobinJY Métais, PA Doerfler, T Mayuranathan, DE Bauer, SC Fowler, MM Hsieh, ...Blood advances 3 (21), 3379-3392, 20191142019
3-) B-cell depletion is protective against anti-AAV capsid immune response: a human subject case studyM Corti, ME Elder, DJ Falk, L Lawson, BK Smith, S Nayak, TJ Conlon, ...Molecular Therapy-Methods & Clinical Development 1, 14033, 20141072014
4-) Oral delivery of Acid Alpha Glucosidase epitopes expressed in plant chloroplasts suppresses antibody formation in treatment of Pompe miceJ Su, A Sherman, PA Doerfler, BJ Byrne, RW Herzog, H DaniellPlant biotechnology journal 13 (8), 1023-1032, 2015662015
5-) Copackaged AAV9 vectors promote simultaneous immune tolerance and phenotypic correction of Pompe diseasePA Doerfler, AG Todd, N Clement, DJ Falk, S Nayak, RW Herzog, ...Human gene therapy 27 (1), 43-59, 2016612016